Project by a team of Oregon Health & Science University
- A team from Oregon Health & Science University used CRISPR-Cas9 for the first time in a human body to cure a rare form of blindness.
- The medicine with CRISPR-Cas9 is developed by a biotech company Editas Medicine.
- During this treatment the CRISPR-Cas9 enzymes were delivered in the eyeball with a fluid like eyedrops.
CRISPR-Cas9, Gene Editing
Why is this a breakthrough?
This is a first CRISPR-Cas9 application in a human body. If this treatment becomes a success it could pave the way for gene editing medicaments.
What are the next project steps?
In the next month the doctors will observe this experiment and if it will prove a success it will be applied to 18 more patients.